Neurodevelopmental evaluation of UPN 12. All functions except gross motor in DDST-II improved by 2 months after infusion. Walking and running steadily improved in GMFM. Self-care, mobility, and social functions increased gradually on PEDI-caregiver assistance scale. DDST-II; Denver developmental screening test II, PEDI; pediatric evaluation of disability inventory, GMFM; gross motor function measure-88.
Lee et al. Journal of Translational Medicine 2012 10:58 doi:10.1186/1479-5876-10-58